Duchenne muscular dystrophy (DMD) is a muscle degeneration disorder caused by mutations affecting the dystrophin gene. Researchers show how a dual CRISPR RNA method restored dystrophin protein ...
In work involving several new generations of mouse model development, Jackson Laboratory (JAX) researchers have tested a therapeutic intervention for spinal muscular atrophy (SMA) that restores some ...
Researchers report on their discovery of a way to bypass faculty cell signalling that leads to muscle damage in Duchene muscular dystrophy. This work suggests a new therapeutic strategy for patients ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback